An Illinois family pushed for both boys to receive the potentially life changing medical treatment after one was approved and the other initially denied by their insurer. Now both boys have received the gene therapy and the family is together in time for Christmas. NBC News’ Maggie Vespa reports. Read more
Nbc News - Dec 24A new class of life-saving drugs is helping children who once had no hope. But some carry a price tag of millions for a single dose, and the American healthcare system hasn't figured out how to pay. Read more
Cbs News - Dec 15A new class of life-saving drugs is helping children who once had no hope. But some carry a price tag of millions for a single dose, and the American health care system hasn't figured out how to pay. Read more
Cbs News - Dec 15
The race to develop safer, longer lasting, and less invasive treatments is accelerating, and at the heart of that challenge lies drug delivery. Read more
Medical News - Nov 27
Oliver has an inherited condition called Hunter syndrome, which causes progressive damage to the body and brain. Read more
The Bbc - Nov 24
PHILADELPHIA, PA — Passage Bio, Inc. (Nasdaq: PASG) reported third-quarter financial results and outlined steady progress across its upliFT-D gene therapy program, positioning the company for critical regulatory and clinical ... Read more
Mychesco - Nov 18
DelveInsight's comprehensive report titled "Cell and Gene Therapy in Parkinson's disease Market Insights, Epidemiology, and Market Forecast - 2034" offers a detailed analysis of Cell and Gene Therapy in Parkinson's disease. The report analyzes the existing treatment practices and unmet Read more
Openpr.com - Nov 16The Food and Drug Administration is adding a new warning to a gene therapy linked to two patient deaths earlier this year. Sarepta Therapeutics' Elevidys will carry the FDA's strongest warning label about the risks of liver damage and liver failure, the agency said Friday. The action follows mont... Read more
Apnews - Nov 14
Use code ONLINE20 to get 20% off on global market reports and stay ahead of tariff changes, macro trends, and global economic shifts.Cell And Gene Therapy Supply Chain/Logistics Market Size Valuation Forecast: What Will the Market Be Worth by 2025?The Read more
Openpr.com - Nov 14
(MedPage Today) -- Personalized vitamin D supplementation -- often requiring 5,000 IU of vitamin D each day -- did prove to have secondary prevention benefits in the TARGET-D randomized trial presented at the American Heart Association meeting... Read more
Medpagetoday - Nov 11